Miglustat for treatment of Niemann-Pick C disease: a randomised

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Last updated 12 fevereiro 2025

Miglustat for treatment of Niemann-Pick C disease: a randomised

Imaging of neuroinflammation in adult Niemann-Pick type C disease

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PDF] Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study

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New therapies in the management of Niemann-Pick type C disease: clinical utility of miglustat

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Niemann-Pick Disease disease: Malacards - Research Articles, Drugs, Genes, Clinical Trials

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